Kebilidi is the first approved gene therapy that can be directly administered to the brain. Its OK secures a priority review ...
The Food and Drug Administration (FDA) has granted accelerated approval to Kebilidi™ (eladocagene exuparvovec-tneq) for the treatment of adult and pediatric patients with aromatic L-amino acid ...
The FDA issued its first stamp of approval for a cell or gene therapy back in 2017 to Novartis' Kymriah. | The gene therapy ...
Medpage Today on MSN19h
First Brain-Delivered Gene Therapy Approved for AADC DeficiencyThe treatment is the first approved gene therapy for AADC deficiency, the FDA said. People with this rare disorder have ...
SEKISUI Diagnostics' microbial CDMO business announces it has completed construction of its £15.7 million ($20.7 million) ...
Gene therapy can effectively treat various diseases, but for some debilitating conditions like muscular dystrophies there is ...
GlobalData on MSN9h
FDA grants accelerated approval for PTC’s AADC deficiency gene therapyThe US Food and Drug Administration (FDA) has granted accelerated approval for PTC Therapeutics’ KEBILIDI, the first gene ...
Enter NAD+, an important molecule in the body responsible for over 500 enzyme functions. It is believed that NAD+ ... Whether you're curious about NAD+ IV therapy or want to know if NAD+ supps can ...
Stockhead on MSN12h
Health Check: Actinogen powers ahead with key Alzheimer’s disease trialActinogen Medical (ASX:ACW) reports that its well-anticipated Alzheimer’s disease clinical trial is on track, with an interim ...
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